Neuren Pharmaceuticals Limited

NURPF · OTC

Company research

Neuren Pharmaceuticals Limited (ASX: NEU; OTC: NURPF) is an Australia-based biopharmaceutical company focused on developing innovative therapies for serious neurodevelopmental disorders that emerge in early childhood. The company's lead product, DAYBUE (trofinetide), has received FDA approval for the treatment of Rett syndrome in adults and pediatric patients aged two years and older, with commercialisation in North America conducted through an exclusive licensing agreement with Acadia Pharmaceuticals Inc. Neuren's second drug candidate, NNZ-2591, is currently progressing through Phase 2 clinical trials targeting a range of rare neurodevelopmental conditions including Phelan-McDermid, Angelman, and Pitt Hopkins syndromes, with all programs having received orphan drug designation in the United States. Incorporated in 2001 and headquartered in Camberwell, Victoria, Australia, Neuren operates across two reportable segments — Commercial Products and Research and Development — and reported total revenue of approximately AUD $224.3 million in 2025.

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